4WHIM: Evaluating the Oral CXCR4 Antagonist Mavorixafor in Patients With WHIM Syndrome via a Global Phase 3, Randomized, Placebo-Controlled Trial With Open-label Extension

JOURNAL OF CLINICAL IMMUNOLOGY(2022)

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关键词
primary immunodeficiency, clinical trial, WHIM syndrome, randomized, myelokathexis, neutropenia, CXCR4
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