CHEMICALLY OPTIMIZED STEREOPURE OLIGONUCLEOTIDES DIRECT ADAR-MEDIATED RNA EDITING OF SERPINA1 TRANSCRIPTS, YIELDING FUNCTIONAL ALPHA-1-ANTITRYPSIN PROTEIN IN A MOUSE MODEL FOR alpha 1-ANTITRYPSIN DEFICIENCYPrashant Monian,Chikdu Shivalila,Genliang Lu,David Boulay,Karley Bussow,Michael Byrne,Jigar Desai,Frank Favaloro,Jack Godfrey,Andrew Hoss,Naoki Iwamoto,Tomomi Kawamoto,Jayakanthan Kumarasamy,Pachamuthu Kandasamy,Anthony Lamattina,Muriel Lemaitre,Amber Lindsey,Richard Looby,Jake Meterville,Tom Pu,Stephany Standley,Snehlata Tripathi,Hailin Yang,Yuan Yin,Hui Yu, Cong Zhou,Paloma Giangrande,Chandra VargeeseHEPATOLOGY(2021)引用 0|浏览19暂无评分AI 理解论文溯源树样例生成溯源树,研究论文发展脉络Chat Paper正在生成论文摘要