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APPLICATION OF REAL-WORLD EVIDENCE ANALYTICS: A 6-YEAR EVENT-FREE SURVIVAL ANALYSIS IN ALAGILLE SYNDROME OF THE GALA CLINICAL RESEARCH DATABASE AND MARALIXIBAT TREATED PATIENTS

Bettina E. Hansen,Shannon M. Vandriel,Pamela Vig,Will Garner,Li-Ting Li,Huiyu She,Jian-She Wang,Melissa A. Gilbert,Irena Jankowska,Piotr Czubkowski,Dorota Gliwicz-Miedzinska,Emmanuel M. Gonzales,Emmanuel Jacquemin,Jerome Bouligand,Nancy Spinner,Kathleen M. Loomes,David A. Piccoli,Lorenzo D'Antiga,Emanuele Nicastro,Etienne Sokal,Tanguy Demaret,Noelle Ebel,Jeffrey A. Feinstein,Rima Fawaz,Silvia Nastasio,Florence Lacaille,Dominique Debray,Henrik Arnell,Bjorn Fischler,Susan Siew,Michael Stormon,Saul J. Karpen,Rene Romero,Kyung Mo Kim,Woo Yim Baek,Winita Hardikar,Sahana Shankar,Amin J. Roberts,Helen M. Evans,M. Kyle Jensen,Marianne Kavan,Shikha S. Sundaram,Alexander Chaidez,Palaniswamy Karthikeyan,Suzanne Davison,Maria Camila Sanchez,Maria Lorena Cavalieri,Henkjan J. Verkade,Way Seah Lee,James E. Squires,Christina Hajinicolaou,Chatmanee Lertudomphonwanit,Ryan T. Fischer,Catherine Larson-Nath,Yael Mozer-Glassberg,Cigdem Arikan,Henry C. Lin,Jesus Quintero Bernabeu,Seema Alam,Deirdre Kelly,Elisa Carvalho,Cristina Targa Ferreira,Giuseppe Indolfi,Ruben E. Quiros-Tejeira,Pinar Bulut,Pier Luigi Calvo,Zerrin Onal,Pamela L. Valentino,Dev M. Desai,John Eshun,Maria Rogalidou,Antal Dezsofi,Sabina Wiecek,Gabriella Nebbia,Raquel Borges Pinto,Victorien M. Wolters,Maria Legarda Tamara,Andreanne N. Zizzo,Jennifer Garcia,Kathleen Schwarz,Marisa Beretta,Thomas Damgaard Sandahl,Carolina Jimenez-Rivera,Nanda Kerkar,Jernej Brecelj,Quais Mujawar,Nathalie Rock,Cristina Molera,Wikrom Karnsakul,Eberhard Lurz,Ermelinda Santos-Silva,Niviann Blondet,Luis Bujanda,Uzma Shah,Richard J. Thompson,Binita M. Kamath

HEPATOLOGY(2021)

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