In utero enzyme replacement therapy in a fetus with infantile-onset Pompe diseaseJennifer L. Cohen,Pranesh Chakraborty,Karen Fung-Kee-Fung,Marisa E. Schwab,Deeksha Bali,Sarah Young,Michael H. Gelb,Hamid Khaledi,Nathan McIntosh,Alicia DiBattista, Deidre Kelly,Stacey Smallshaw,Billie Lianoglou,Paul Harmatz,Priya S. Kishnani,Tippi C. MacKenzieMolecular Genetics and Metabolism(2022)引用 0|浏览14暂无评分AI 理解论文溯源树样例生成溯源树,研究论文发展脉络Chat Paper正在生成论文摘要