Efficacy and Safety of Vamorolone in Duchenne Muscular Dystrophy

Jean K. Mah,Paula R. Clemens,Michela Guglieri,Edward C. Smith,Richard S. Finkel,Mar Tulinius,Yoram Nevo,Monique M. Ryan,Richard Webster,Diana Castro,Nancy L. Kuntz,Craig M. McDonald,Jesse M. Damsker,Benjamin D. Schwartz,Laurel J. Mengle-Gaw,Stefan Jackowski,Georgia Stimpson,Deborah A. Ridout,Vandana Ayyar-Gupta,Giovanni Baranello,Adnan Y. Manzur,Francesco Muntoni,Heather Gordish-Dressman,Mika Leinonen,Leanne M. Ward,Eric P. Hoffman,Utkarsh J. Dang,Francesco Muntoni,Adnan Manzur,Giovanni Baranello,Stephanie Robb, Ros Quinlivan,Anna Sarkozy,Pinki Munot,Marion Main, Lianne Abbot,Volker Straub,Michela Guglieri, Chiara Bertolli,Anna Mayhew,Robert Muni-Lofra,Meredith James, Jassi Sodhi, Deepak Parasuraman, Zoya Alhaswani, Heather McMurchie, Rosanna Rabb,Anne-Marie Childs,Karen Pysden, Lindsey Pallant, Tiffany Small,Stefan Spinty, Rajesh Madhu, Alison Shillington, Sarah Gregson,Elizabeth Wraige,Heinz Jungbluth,Vasantha Gowda,Jennie Sheehan,Imelda Hughes, Sinead Warner, Emily Davies,Tracey Willis,Richa Kulshrestha, Nicholas Emery, Kate Strachan,Min Ong, Kay White, Kate Skone, Frances Gibbon, Bethan Parsons,Anirban Majumdar, Kayal Vijaykumar, Faye Mason, Claire Frimpong-Ansah, Karen Naismith, Julie Burslem,Iain Horrocks,Marina Di Marco,Sarah Brown, Sarah Williamson, Kirstie Spencer, Gabby Chow,Christian de Goede, Andrea Selley, Neil Thomas,Marjorie Illingworth, Michelle Greary, Jenni Palmer, Cathy White, Kate Greenfield, Grainne Nic Fhirleinn, Melanie Douglas, Sandya Tiraputhi, Nahin Hussain, Yvonne Julien, Gautam Ambegaonkar, Deepa Krishnakumar, Jacqui Taylor, Jane Tewnion, Elma Stephens, Saleel Chandratre, Sithara Ramdas, Hayley Ramjattan,Alex Baxter, Clare Eadie,Craig M McDonald,Erik K Henricson,R Ted Abresch,Nanette C Joyce, Venkatarman Viswanathan, Sivaprakasam Chidambaranathan,Douglas Biggar,Laura C McAdam,Jean K Mah,Mar Tulinius,Avital Cnaan,Lauren P Morgenroth,Robert Leshner,Carolina Tesi-Rocha,Mathula Thangarajh,Tina Duong,Andrew Kornberg,Monique Ryan,Yoram Nevo,Alberto Dubrovsky,Paula R Clemens,Hoda Abdel-Hamid,Anne M Connolly,Alan Pestronk,Jean Teasley,Tulio E Bertorini,Richard Webster,Hanna Kolski,Nancy Kuntz, Sherilyn W Driscoll,John B Bodensteiner, Jose Carlo,Ksenija Gorni, Timothy Lotze,John W Day,Peter Karachunski

JAMA Network Open(2022)

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