O-02 Phase 3 PRISM trials : Update on pegvaliase treatment efficacy and safety for adult phenylketonuria ○

semanticscholar(2019)

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摘要
O-02 Phase 3 PRISM trials: Update on pegvaliase treatment efficacy and safety for adult phenylketonuria ○ Mitsuhiro Kuwahara1, Cary O. Harding2, Deborah Bilder3, John Posner4, Harvey Levy5, Orli Rosen6 Mingjin Li6, Joy Olbertz6, Haoling H Weng6 1BioMarin Pharmaceutical Japan K.K. 2Oregon Health & Science University, Portland, OR, USA 3University of Utah, Salt Lake City, UT, USA 4King’s College London, London, UK 5Boston Children’s Hospital, Boston, MA, USA 6BioMarin Pharmaceutical Inc., Novato, CA, USA
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