First Proof-Of-Concept Of Miqure (Tm) Based Gene Targeting In The Liver: Lipid Lowering And Atherosclerosis Suppression By Aav-Miqure (Tm)-Mediated Angptl3 Targeting

Vanessa Zancanella, Astrid Valles-Sanchez, Carlos Vendrell Tornero, Maroeska Oudshoorn-Dickmann, Hendrina Wattimury,Kristel Van Rooijen, Mark Van Veen,Monika Golinska,Elsbet J. Pieterman,Nanda Keijzer,Hans M. G. Princen,Geurt Stokman,Martin De Haan,Ying Poi Liu

MOLECULAR THERAPY(2021)

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