Targeted Genome Editing of Haematopoietic Stem Cells for Treating Recombination Activating Gene 1 (RAG1) ImmunodeficiencyM. C. Castiello,N. Sacchetti,C. Brandas,S. Porcellini,S. Ferrari,E. Draghici,V. Vavassori,D. Minuta,M. Di Verniere,A. Jacob, L. Sergi Sergi,M. Bosticardo,L. D. Notarangelo, P. Genovese,L. Naldini,A. VillaMOLECULAR THERAPY(2021)引用 0|浏览12暂无评分AI 理解论文溯源树样例生成溯源树,研究论文发展脉络Chat Paper正在生成论文摘要