Gene Therapy For Fanconi Anemia [Group A]: Preliminary Results Of Ongoing Rp-L102 Clinical Trials
Agnieszka Czechowicz,Julian Sevilla,Claire Booth,Rajni Agarwal,Josune Zubicaray,Paula Rio,Susana Navarro,Phil J. Ancliff,Brian C. Beard,Kenneth M. Law,Grace Choi,Miriam Zeini,Camilla Duran-Persson,Eileen Nicoletti,Gayatri R. Rao,John E. Wagner,Jonathan Schwartz,Juan A. Bueren,Maria Grazia Roncarolo MOLECULAR THERAPY(2021)
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