Comparison Of Cognitive Function In Siblings With Neuronopathic Mucopolysaccharidosis Type Ii: Evaluation Of Early Treatment With Intravenous Idursulfase And Intrathecal Idursulfase-It
MOLECULAR GENETICS AND METABOLISM(2021)
关键词
neuronopathic mucopolysaccharidosis type ii,intravenous idursulfase,cognitive function
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