AAV.U7-snRNA-Mediated Exon Skipping of the Toxic DUX4 Gene as a Promising Therapeutic Approach for Facioscapulohumeral Muscular DystrophyAfrooz Rashnonejad, Allison R. Fowler, Nettie K. Pyne,Gholamhossein Amini Chermahini,Andrew Palo,Madison A. Harper,Carlee R. Giesige,Nicolas Wein,Scott Q. HarperMOLECULAR THERAPY(2018)引用 0|浏览1暂无评分AI 理解论文溯源树样例生成溯源树,研究论文发展脉络Chat Paper正在生成论文摘要