Efficient In Vitro and In Vivo Self-Repression of Spcas9 Gene and Reduction of Off-Target Mutations Using a Molecular Hara-Kiri Method

Jacques P. Tremblay, Jean-Paul Iyombe-Engembe,Benjamin Duchene,Joel Rousseau,Dominique Ouellet,Khadija Cherif,Antoine Guyon

MOLECULAR THERAPY(2019)

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