PR006, an AAV Gene Therapy Vector Expressing Progranulin, Improved FTD-GRN Phenotypes In Vitro and In VivoLaura D. Heckman,Suzanne R. Burstein,Alissa Brandes,Li Chin Wong,Zhaohui Yang,Hsuan-Ni Lin,Tim Fenn,Stuart Nelson,Zarah Aziz,Sid Kamalakaran,Swetha Garimalla,Jorge Haller,Jenn Daily,Jason Politi,Yong Dai,Franz Hefti,Asa AbeliovichMOLECULAR THERAPY(2020)引用 0|浏览2暂无评分AI 理解论文溯源树样例生成溯源树,研究论文发展脉络Chat Paper正在生成论文摘要