AAV-Mediated Gene Therapy to Treat Mucopolysaccharidosis Type IVA in a New Morquio a Mouse ModelVictor Sanchez,Joan Bertolin,Albert Ribera,Xavier Sanchez,Sara Marco,Sandra Motas,Jennifer Perez,Carles Roca,Gemma Elias,Miquel Garcia,Xavier Leon,Virginia Haurigot,Jesus Ruberte,Fatima BoschMOLECULAR THERAPY(2020)引用 0|浏览35暂无评分AI 理解论文溯源树样例生成溯源树,研究论文发展脉络Chat Paper正在生成论文摘要