A Universal Gene Correction Approach for FKRP Mutant Patient-Specific iPS Cells: Potential for Autologous Cell TherapyNeha Dhoke,Hyunkee Kim,Sridhar Selvaraj,Carolina Ortiz-Cordero,Nelio A. J. Oliveira,James Kiley,Qi Long Lu,Anne Bang,Rita PerlingeiroMOLECULAR THERAPY(2020)引用 0|浏览5暂无评分AI 理解论文溯源树样例生成溯源树,研究论文发展脉络Chat Paper正在生成论文摘要