A Novel Base Editing Approach to Directly Edit the Causative Mutation in Sickle Cell Disease
S. Haihua Chu,Michael S. Packer,Jenny R. Olins,Genesis Lung,Lo-I Cheng,Alexander Liquori,Calvin Lee,Jeffrey Marshall,Bo Yan,Jeremy Decker,Bob Gantzer,Ling Lin,Luis Barrera,Daisy Lam,Conrad Rinaldi,Adrian P. Rybak,Minerva Sanchez,Yeh-Chuin Poh,Sarah Smith,Scott J. Haskett,Ian Slaymaker,Nicole Gaudelli,Carlo Zambonelli,Manmohan Singh,Adam Hartigan,Giuseppe Ciaramella MOLECULAR THERAPY(2020)
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