Gene Correction Using CRISPR/Cas9: IND-Enabling Studies to Support a Clinical Trial of a CRISPR/Homology-Directed Repair Treatment for Sickle Cell DiseaseMark A. DeWitt,Wendy Magis,Stacia K. Wyman,Dario Boffelli,Zulema Romero,Jonathan Vu,Seok-Jin Heo,Suzanne Said, Fiona Hennig,Alejandra Davila,Jack Mottahedeh,Beatriz C. Fernandez,Matthew McNeill,Garrett R. Rettig,Yongming Sun,Patrick J. Lau,Yu Wang,Mark A. Behlke,Fyodor Urnov,Donald B. Kohn,Jacob E. Corn,David I. K. Martin,Mark C. WaltersMOLECULAR THERAPY(2020)引用 1|浏览19暂无评分AI 理解论文溯源树样例生成溯源树,研究论文发展脉络Chat Paper正在生成论文摘要