Intrathecal scAAV9 Gene Therapy Is an Effective Treatment for PPT1-Deficiency in the Preclinical INCL Mouse ModelAlejandra J. Rozenberg,Erik A. Lykken,Steven J. GrayMOLECULAR THERAPY(2017)引用 0|浏览5暂无评分AI 理解论文溯源树样例生成溯源树,研究论文发展脉络Chat Paper正在生成论文摘要