Updated Results of a European Gene Therapy Trial in Fanconi Anemia Patients, Subtype A
Paula Rio,Susana Navarro,Rebeca Sanchez-Dominguez,Jose C. Segovia,Wei Wang,Eva Merino,Rosa M. Yanez,Jose A. Casado,Yari Gimenez,Francisco J. Roman-Rodriguez,Omaira Alberquilla,Eva Galvez, Josune Zubicarai,Jordi Barquinero,Anne Galy,Nagore Garcia De Andoin,Ricardo Lopez,Albert Catala,Francois Lefrere,Marina Cavazzana,Jonathan D. Schwartz,Roser M. Pujol,Jordi Surralles,Jean Soulier,Manfred Schmidt,Cristina Diaz De Heredia,Julian Sevilla,Juan A. Bueren MOLECULAR THERAPY(2020)
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