Rationale and Design of NEURO-TTRansform, a phase 3 study evaluating the efficacy and safety of AKCEA-TTR-LRx in patients with hereditary transthyretin-mediated Amyloid Polyneuropathy (hATTR-PN)

L. Tai,L. Obici, J. Giilmore, N. Viney,C. Monteiro, G. Buchele,M. Brambatti, S. Tskimikas, S. Jung, L. O'dea,E. Schneider, R. Geary,B. Monia

EUROPEAN JOURNAL OF NEUROLOGY(2020)

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