Update on safety and efficacy of lentiviral haematopoietic stem cell gene therapy (HSC-GT) for metachromatic leukodystrophy (MLD)
V. Calbi,F. Fumagalli,L. Lorioli,M. Sessa, M. E. Bernardo,F. Cugnata, P. M. V. Roncoita, S. Acquati, D. Redaelli, V. Attanasio, R. Penati,M. P. Cicalese,F. Ferrua,F. Barzaghi,M. Migliavacca,F. Tucci,A. Assanelli,P. Silvani, F. Silvani,M. Facchini, S. Zancan,F. Ciotti,M. Sarzana,A. Zambon,A. Calabria,E. Montini,S. Canale,G. Antonioli, M. Gabaldo,I. D. Lopez,F. Morena, A. Quattrini,C. Baldoli,S. Martino,C. Di Serio, F. Ciceri,M. G. Natali Sora,L. Naldini,A. Biffi,A. Aiuti HUMAN GENE THERAPY(2017)
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