Gene therapy trial in non-conditioned Fanconi anemia patients
P. Rio,S. Navarro,W. Wang,R. Sanchez-Dominguez,E. Merino,J. C. Segovia,A. Galy,M. L. Lamana, R. M. Yanez,J. A. Casado, Y. Gimenez, F. J. Roman-Rodriguez,L. Alvarez,R. M. Pujol,J. Surralles,R. Lopez,N. Garcia de Andoin,A. Catala,E. Galvez,R. Hladun,J. D. Schwartz,M. Schmidt,C. Diaz de Heredia,J. Sevilla, J. Bueren HUMAN GENE THERAPY(2018)
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