Robust SOD1 knockdown in large mammal spinal cord using a novel delivery paradigm with AAV gene therapy targeting SOD1 for the treatment of SOD1-ALS H. Patzke,Q. Chen,J. Carroll,R. Wang, P. Zhou,C. Huang,X. Wang,J. Aubin,M. Nonnenmacher, X. Ren,W. Wang,E. Christensen,B. Johnson,L. Liu,T. Nguyen, R. Zhou,M. Hossbach,J. Deckert, F. Chen,J. Thompson,T. Federici,N. M. Boulis,J. Hou,D. SahHUMAN GENE THERAPY(2018)引用 3|浏览27暂无评分AI 理解论文溯源树样例生成溯源树,研究论文发展脉络Chat Paper正在生成论文摘要