Allele specific genome editing rescues cystic fibrosis splicing mutations in patients organoidsG. Maule,A. Casini,C. Montagna,D. Arosio,A. Ramalho,Z. Debyser,M. Carlon,G. Petris,A. CeresetoHUMAN GENE THERAPY(2018)引用 0|浏览14暂无评分AI 理解论文溯源树样例生成溯源树,研究论文发展脉络Chat Paper正在生成论文摘要