Correction of Gb3 levels in alpha-Galactosidase A deficient mice by enzyme produced in vivo by shielded engineered cells E. Makino, B. Fluharty, D. Tietz,M. Donovan, E. Pearson,L. Barney,J. Sewell, M. McAulife, S. Shrestha,J. Huang,R. Newman, O. O'Conner, T. Glyptis, C. Sparages, V. Zhao, S. Brittes Boss, K. Barret, M. Gorgievski,D. Moller, D. Gorzo, D. Peritt, R. VivaldiHUMAN GENE THERAPY(2019)引用 0|浏览7暂无评分AI 理解论文溯源树样例生成溯源树,研究论文发展脉络Chat Paper正在生成论文摘要