From genetics to therapy: successful one-year eculizumab treatment of protein-losing enteropathy caused by loss of the complement regulator CD55

A. Kurolap, O. Eshach-Adiv,T. Hershkovitz,T. Paperna,A. Mory, D. Oz-Levi,Y. Zohar,H. Mandel,J. Chezar, D. Azoulay, S. Peleg,E. E. Half,V. Yahalom, L. Finkel, O. Weissbrod,D. Geiger, A. Tabib,R. Shaoul,D. Magen,L. Bonstein, D. Mevorach, H. N. Baris

EUROPEAN JOURNAL OF HUMAN GENETICS(2019)

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