Autologous Ex Vivo Lentiviral Gene Therapy for the Treatment of Severe Combined Immune Deficiency Due to Adenosine Deaminase Deficiency
Donald B. Kohn,Kit L. Shaw,Elizabeth K. Garabedian,Denise A. Carbonaro-Sarracino,Theodore B. Moore,Satiro De Oliveira,Gay M. Crooks,John Tse,Sally Shupien,Dayna Terrazas,Alejandra Davila,Amalia Icreverzi,Allen Yu,Provaboti Barman,Maritess Coronel,Beatriz Campo Fernandez,Ruixue Zhang,Roger Hollis,Chilenwa Uzowuru,Hilory Ricketts,Jinhua Xu-Bayford,Valentina Trevisan,Serena Arduini,Frances Lynn,Mahesh Kudari,Andrea Spezzi,Lilith Reeves,Kenneth Cornetta,Robert Sokolic,Roberta Parrott,Rebecca Buckley,Claire Booth,Fabio Candotti,Harry L. Malech,Adrian J. Thrasher,H. Bobby Gaspar JOURNAL OF CLINICAL IMMUNOLOGY(2019)
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