Antisense oligonucleotide targeting glycogen synthase (GYS1) in a Pompe disease mouse modelVirginia E. Kimonis,Lan Weiss,Michele Carrer,Lac Ta, Mindy Chang,Cheng Cheng,Lisa Hettrick,Andy Watt,Nina Raben,Tamar GrossmanMOLECULAR GENETICS AND METABOLISM(2020)引用 0|浏览15暂无评分AI 理解论文溯源树样例生成溯源树,研究论文发展脉络Chat Paper正在生成论文摘要