Erratum: Long-Term Metabolic Correction of Phenylketonuria by AAV-Delivered Phenylalanine Amino Lyase.

Molecular Therapy - Methods & Clinical Development(2022)

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摘要
[This corrects the article DOI: 10.1016/j.omtm.2019.12.014.].
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关键词
phenylketonuria,adeno-associated virus,phenylalanine amino lyase,gene therapy
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