A phase 1/2 clinical trial of systemic gene transfer of scAAV9.U1a.hSGSH for MPS IIIA: safety, tolerability, and preliminary evidence of biopotencyKevin M. Flanigan,Kristen V. Truxal,Kim L. McBride,Kelly A. McNally, Krista L. Kunkler,Nicholas A. Zumberge,Lisa Martin,Shawn Aylward,Marco Corridore,Christopher McKee,Tabatha R. Simmons,Haiyan Fu,Douglas M. McCartyMolecular Genetics and Metabolism（2017）引用 3|浏览25暂无评分AI 理解论文溯源树样例生成溯源树，研究论文发展脉络Chat Paper正在生成论文摘要
