Rescue of mouse Prkdc scid deficiency by transplantation of gene-repaired haematopoietic stem cells
H H Abdulrazak,C Rocca,S J Howe,M Eugenia Alonsoferrero,Richard Gabriel,Cynthia C Bartholomae,Chv Gan,Marina I Garin,F Javier Molinaestevez,A C Roberts,Michael P Blundell,G Gueenechea,Michael C Holmes,Philip D Gregory,C Kinnon,C Von Kalle,Manfred G Schmidt,Juan A Bueren,Adrian J Thrasher,Rafael J Yanezmunoz HUMAN GENE THERAPY(2013)
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