P3.12 Small molecule compounds that correct alternative splicing of the SMN2 gene and restore SMN protein expression and function
M Woll,Seunghee Lee,Sungyool Choi,Hiroo Koyama,T Yang,Guanxing Chen,Siyu Zhang,Na Zhang,Sheng Huang,Chunyan Li,Anthony Turpoff, Joseph A Hedrick,Xiang Zhao,Anna Mollin, M Zadel,S Letinski,H Qi,B Furia,P Vazirani,James H Crona,Sungtae Jung,A Dakka,Jana Narasimhan,Nikolai Naryshkin,Joseph M Colacino,Panayiota Trifillis,O Khwaja, I Gerlach,Hasane Ratni,F Metzger,Ke Chen,Ellen M Welch,Marla Weetall,Gary Mitchell Karp,Stuart W Peltz,Neil G Almstead,John Babiak,Kathleen D Mccarthy,D Kobayashi,Sergey Paushkin,Michael R Haley,V Gabbeta Neuromuscular Disorders(2011)
关键词
protein expression,alternative splicing
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