基本信息
浏览量:180
职业迁徙
个人简介
She was the principal investigator leading the successful gene therapy trial for SCID patients who lack an enzyme critical to DNA synthesis (ADA-SCID), which has received European Commission approval to market under the name of Strimvelis. Under her direction, the San Raffaele Scientific Institute has been seminal in showing the efficacy of gene therapy for otherwise untreatable inherited metabolic diseases and primary immunodeficiencies.
Dr. Roncarolo established the Stanford Center for Definitive and Curative Medicine to cure patients with currently incurable diseases through the development of innovative stem cell-and gene-based therapies.
Dr. Roncarolo established the Stanford Center for Definitive and Curative Medicine to cure patients with currently incurable diseases through the development of innovative stem cell-and gene-based therapies.
研究兴趣
论文共 582 篇作者统计合作学者相似作者
按年份排序按引用量排序主题筛选期刊级别筛选合作者筛选合作机构筛选
时间
引用量
主题
期刊级别
合作者
合作机构
MOLECULAR THERAPY METHODS & CLINICAL DEVELOPMENTno. 1 (2024)
bioRxiv the preprint server for biology (2024)
JOURNAL OF ALLERGY AND CLINICAL IMMUNOLOGYno. 3 (2024): 595-605
Yael Gernez,Bindu Sathi,Juanita Valdes Camacho, Latha Rao, Berthil Glader,Deepika Singh,Elisabeth Hoyte,David Lewis,Maria Grazia Roncarolo,May Chien,Rosa Bacchetta,Katja Weinacht
Journal of Allergy and Clinical Immunologyno. 2 (2024): AB186
Leukemiano. 6 (2024): 1246-1255
Transplantation and Cellular Therapyno. 2 (2024): S13
Alma-Martina Cepika,Laura Amaya,Colin Waichler,Mansi Narula,Benjamin C. Thomas,Pauline P. Chen, Michelle M. Mantilla,Mara Pavel-Dinu, Robert Freeborn,Matthew H. Porteus,Rosa Bacchetta,Fabian Mueller,
MOLECULAR THERAPYno. 4 (2023): 370-371
引用0浏览0引用
0
0
David C. Shyr,Robert Lowsky, Weston Miller,Mark A. Schroeder, Tonia Buchholz,Kirstin Dougall,Allison Intondi,Alexandra Charles, Josh Lehrer,Ali Bouge,Stacey Wolf, Blair MacDonald,
Bloodno. Supplement 1 (2023): 5000-5000
PEDIATRIC BLOOD & CANCERno. 4 (2023): 118-119
引用0浏览0引用
0
0
加载更多
作者统计
#Papers: 587
#Citation: 52045
H-Index: 104
G-Index: 222
Sociability: 8
Diversity: 4
Activity: 81
合作学者
合作机构
D-Core
- 合作者
- 学生
- 导师
数据免责声明
页面数据均来自互联网公开来源、合作出版商和通过AI技术自动分析结果,我们不对页面数据的有效性、准确性、正确性、可靠性、完整性和及时性做出任何承诺和保证。若有疑问,可以通过电子邮件方式联系我们:report@aminer.cn